Clinical Trial, Phase IHumanClinical Trial, Phase I

A phase 1/2a follistatin gene therapy trial for becker muscular dystrophy

Molecular therapy : the journal of the American Society of Gene Therapy, 2015 Jan. Mendell JR, Sahenk Z, Malik V and 17 others.

Study type

Clinical trial · Clinical Trial, Phase I

Subjects

Human participants (PubMed MeSH: Humans)

Journal

Molecular therapy : the journal of the American Society of Gene Therapy

Published

2015 Jan

PubMed

PMID 25322757 ↗

DOI

10.1038/mt.2014.200 ↗

Full text

Free on PubMed Central (PMC4426808) ↗

Where PepCue cites this

This paper is part of the evidence base behind this profile. Citing a study is not an endorsement of the compound: papers that found no effect are indexed the same way.

Follistatin-344 →

Indexed under

MeSH terms assigned by the National Library of Medicine.

AdultDependovirusDystrophinFollistatin-Related ProteinsGene ExpressionGenetic TherapyGenetic VectorsHumansInjections, IntramuscularMaleMuscle, SkeletalMuscular Dystrophy, Duchenne

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